Niemann-Pick Disease Type C1 - 25 Studies Found
Terminated |
: Safety Study of rhASM Enzyme Replacement Therapy in Adults With Acid Sphingomyelinase Deficiency (Niemann-Pick Disease) :
: 2006-12-11 :
|
Completed |
: Saccadic Eye Movements in Patients With Niemann-Pick Type C Disease : Niemann Pick Diseases : 2006-04-19 : Drug: OGT918 |
Recruiting |
: Investigating Lysosomal Storage Diseases in Minority Groups :
|
Completed |
: Stem Cell Transplant for Inborn Errors of Metabolism :
|
Completed |
: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation :
|